RGNX Chart
About

REGENXBIO Inc., a clinical-stage biotechnology company, provides gene therapies that deliver functional genes to cells with genetic defects in the United States. Its gene therapy product candidates are based on NAV Technology Platform, a proprietary adeno-associated virus gene delivery platform. The company's products in pipeline includes ABBV-RGX-314 for the treatment of wet age-related macular degeneration, diabetic retinopathy, and other chronic retinal diseases; and RGX-202 for the treatment of Duchenne muscular dystrophy, as well as RGX-121 for the treatment of mucopolysaccharidosis type II. It also develops RGX-111 for the treatment of mucopolysaccharidosis type I. In addition, the company licenses its NAV Technology Platform to other biotechnology and pharmaceutical companies. Further, it has a collaboration and license agreement with AbbVie Global Enterprises Ltd. to develop ABBV-RGX-314 outside the United States. REGENXBIO Inc. was incorporated in 2008 and is headquartered in Rockville, Maryland.

Fundamentals
Scroll to Statements
Sector Healthcare Industry Biotechnology Market Cap 532.55M
Enterprise Value 566.19M Income -193.88M Sales 170.44M
Book/sh 2.02 Cash/sh 4.46 Dividend Yield —
Payout 0.00% Employees 371 IPO —
P/E — Forward P/E -4.83 PEG —
P/S 3.12 P/B 5.21 P/C —
EV/EBITDA -3.89 EV/Sales 3.32 Quick Ratio 2.27
Current Ratio 2.38 Debt/Eq 253.59 LT Debt/Eq —
EPS (ttm) -3.46 EPS next Y -2.18 EPS Growth —
Revenue Growth 43.00% Earnings 2026-05-11 ROA -21.93%
ROE -107.00% ROIC — Gross Margin -45.86%
Oper. Margin -189.99% Profit Margin -113.75% Shs Outstand 50.62M
Shs Float 43.00M Short Float 14.38% Short Ratio 5.13
Short Interest — 52W High 16.19 52W Low 5.04
Beta 1.14 Avg Volume 967.85K Volume 140.31K
Target Price $27.82 Recom Buy Prev Close $10.38
Price $10.52 Change 1.35%
Valuation Models

Price estimates from analyst targets and simple models.

1. Analyst consensus
$27.82
Mean price target
2. Current target
$10.52
Latest analyst target
3. DCF / Fair value
$-28.37
Simplified: (Free Cash Flow ÷ Shares) × 18 (P/FCF multiple). Not a …
Ratings
Current target
$10.52
Low
$12.00
High
$50.00
Mean
$27.82

Latest analyst rating changes

Date Action Analyst Rating Change Price Target
2026-03-09 main HC Wainwright & Co. Buy → Buy $30
2026-03-06 main Morgan Stanley Overweight → Overweight $17
2026-02-10 main HC Wainwright & Co. Buy → Buy $32
2026-02-10 main Goldman Sachs Neutral → Neutral $12
2026-02-10 main Morgan Stanley Overweight → Overweight $18
2026-02-10 main Chardan Capital Buy → Buy $50
2026-01-29 main Chardan Capital Buy → Buy $52
2025-12-19 main Stifel Buy → Buy $45
2025-12-15 main Leerink Partners Outperform → Outperform $20
2025-11-20 main Chardan Capital Buy → Buy $52
2025-11-07 main RBC Capital Outperform → Outperform $19
2025-10-07 reit HC Wainwright & Co. Buy → Buy $34
2025-09-08 reit HC Wainwright & Co. Buy → Buy $34
2025-09-08 main Chardan Capital Buy → Buy $52
2025-08-19 reit HC Wainwright & Co. Buy → Buy $34
2025-08-08 main RBC Capital Outperform → Outperform $17
2025-08-08 main Barclays Overweight → Overweight $37
2025-08-08 main Chardan Capital Buy → Buy $52
2025-06-09 main Chardan Capital Buy → Buy $52
2025-04-17 main Goldman Sachs Neutral → Neutral $12
Insider Transactions
Date Shares Value Url Text Insider Position Transaction Start Date Ownership
0 225000 2945250 — Conversion of Exercise of derivative security at price 13.09 per share. MILLS KENNETH THOMAS Director — 2026-01-27 00:00:00 D
1 144864 — — Stock Award(Grant) at price 0.00 per share. SIMPSON CURRAN M Chief Executive Officer — 2026-01-06 00:00:00 D
2 73749 — — Stock Award(Grant) at price 0.00 per share. CHRISTMAS PATRICK J. II Officer — 2026-01-06 00:00:00 D
3 65847 — — Stock Award(Grant) at price 0.00 per share. PAKOLA STEPHEN J Officer — 2026-01-06 00:00:00 D
4 73749 — — Stock Award(Grant) at price 0.00 per share. CHAN MITCHELL Chief Financial Officer — 2026-01-06 00:00:00 D
5 65847 — — Stock Award(Grant) at price 0.00 per share. MALZAHN CRAIG Chief Technology Officer — 2026-01-06 00:00:00 D
6 20811 262635 — Sale at price 12.62 per share. SIMPSON CURRAN M Chief Executive Officer — 2025-10-09 00:00:00 D
7 7624 76469 — Sale at price 10.03 per share. SIMPSON CURRAN M Chief Executive Officer — 2025-09-29 00:00:00 D
8 7734 77495 — Sale at price 10.02 per share. SIMPSON CURRAN M Chief Executive Officer — 2025-09-10 00:00:00 D
9 7768 — — Stock Award(Grant) at price 0.00 per share. STUMP DAVID CARTER Director — 2025-05-30 00:00:00 D
Financials
Line Item2024-12-312023-12-312022-12-312021-12-31
TaxEffectOfUnusualItems0.006.53K1.61K647.82K
TaxRateForCalcs0.000.000.000.09
NormalizedEBITDA-214.86M-250.78M-249.62M170.26M
TotalUnusualItems16.63M11.32M5.38M6.83M
TotalUnusualItemsExcludingGoodwill16.63M11.32M5.38M6.83M
NetIncomeFromContinuingOperationNetMinorityInterest-227.10M-263.49M-280.32M127.84M
ReconciledDepreciation16.21M17.32M12.91M9.56M
ReconciledCostOfRevenue33.57M37.21M54.55M51.83M
EBITDA-198.23M-239.46M-244.24M177.09M
EBIT-214.44M-256.78M-257.15M167.52M
NetInterestIncome-12.48M-6.84M-22.91M-25.56M
InterestExpense12.66M6.86M23.25M26.28M
InterestIncome174.00K25.00K342.00K719.00K
NormalizedIncome-243.73M-274.81M-285.70M121.66M
NetIncomeFromContinuingAndDiscontinuedOperation-227.10M-263.49M-280.32M127.84M
TotalExpenses314.57M358.37M375.60M310.37M
TotalOperatingIncomeAsReported-233.35M-268.13M-262.88M159.98M
DilutedAverageShares49.51M43.73M43.15M43.91M
BasicAverageShares49.51M43.73M43.15M42.44M
DilutedEPS-4.59-6.02-6.502.91
BasicEPS-4.59-6.02-6.503.01
DilutedNIAvailtoComStockholders-227.10M-263.49M-280.32M127.84M
NetIncomeCommonStockholders-227.10M-263.49M-280.32M127.84M
NetIncome-227.10M-263.49M-280.32M127.84M
NetIncomeIncludingNoncontrollingInterests-227.10M-263.49M-280.32M127.84M
NetIncomeContinuousOperations-227.10M-263.49M-280.32M127.84M
TaxProvision0.00-152.00K-84.00K13.41M
PretaxIncome-227.10M-263.65M-280.40M141.25M
OtherIncomeExpense16.63M11.32M5.38M6.83M
SpecialIncomeCharges-2.10M0.000.00
ImpairmentOfCapitalAssets2.10M0.000.00
GainOnSaleOfSecurity18.73M11.32M5.38M6.83M
NetNonOperatingInterestIncomeExpense-12.48M-6.84M-22.91M-25.56M
InterestExpenseNonOperating12.66M6.86M23.25M26.28M
InterestIncomeNonOperating174.00K25.00K342.00K719.00K
OperatingIncome-231.25M-268.13M-262.88M159.98M
OperatingExpense281.01M321.16M321.06M258.53M
OtherOperatingExpenses865.00K397.00K-6.68M333.00K
ProvisionForDoubtfulAccounts-5.00M0.000.00-2.57M
ResearchAndDevelopment208.52M232.27M242.45M181.44M
SellingGeneralAndAdministration76.62M88.49M85.28M79.33M
GeneralAndAdministrativeExpense76.62M88.49M85.28M79.33M
OtherGandA76.62M88.49M85.28M79.33M
GrossProfit49.76M53.03M58.18M418.51M
CostOfRevenue33.57M37.21M54.55M51.83M
TotalRevenue83.33M90.24M112.72M470.35M
OperatingRevenue83.33M90.24M112.72M470.35M
Line Item2023-12-31
TreasurySharesNumber0.00
OrdinarySharesNumber49.55M44.05M43.30M42.83M
ShareIssued49.55M44.05M43.30M42.83M
TotalDebt82.03M89.29M94.80M86.68M
TangibleBookValue259.65M311.74M516.20M764.30M
InvestedCapital259.65M311.74M516.20M764.30M
WorkingCapital174.81M204.70M285.54M388.35M
NetTangibleAssets259.65M311.74M516.20M764.30M
CapitalLeaseObligations82.03M89.29M94.80M86.68M
CommonStockEquity259.65M311.74M516.20M764.30M
TotalCapitalization259.65M311.74M516.20M764.30M
TotalEquityGrossMinorityInterest259.65M311.74M516.20M764.30M
StockholdersEquity259.65M311.74M516.20M764.30M
GainsLossesNotAffectingRetainedEarnings-741.00K-4.43M-15.40M-2.57M
RetainedEarnings-932.15M-705.05M-441.55M-161.23M
AdditionalPaidInCapital1.19B1.02B973.14M928.10M
CapitalStock5.00K4.00K4.00K4.00K
CommonStock5.00K4.00K4.00K4.00K
PreferredStock0.000.000.000.00
TotalLiabilitiesNetMinorityInterest206.34M262.23M317.07M349.61M
TotalNonCurrentLiabilitiesNetMinorityInterest103.14M131.96M186.64M219.13M
OtherNonCurrentLiabilities29.01M49.73M97.84M134.21M
NonCurrentDeferredLiabilities0.00
NonCurrentDeferredRevenue0.00
LongTermDebtAndCapitalLeaseObligation74.13M82.22M88.80M84.93M
LongTermCapitalLeaseObligation74.13M82.22M88.80M84.93M
CurrentLiabilities103.19M130.27M130.43M130.47M
OtherCurrentLiabilities34.31M50.57M48.60M37.89M
CurrentDeferredLiabilities115.00K148.00K1.83M3.33M
CurrentDeferredRevenue115.00K148.00K1.83M3.33M
CurrentDebtAndCapitalLeaseObligation7.90M7.07M6.00M1.75M
CurrentCapitalLeaseObligation7.90M7.07M6.00M1.75M
PensionandOtherPostRetirementBenefitPlansCurrent17.61M18.15M18.07M19.85M
PayablesAndAccruedExpenses43.26M54.34M55.94M67.65M
CurrentAccruedExpenses20.46M31.56M28.72M44.94M
Payables22.80M22.79M27.21M22.71M
TotalTaxPayable0.0011.32M
IncomeTaxPayable0.0011.32M
AccountsPayable22.80M22.79M27.21M11.39M
TotalAssets465.99M573.97M833.27M1.11B
TotalNonCurrentAssets187.99M239.00M417.29M595.08M
OtherNonCurrentAssets6.03M6.84M8.43M8.46M
NonCurrentAccountsReceivable474.00K701.00K1.50M2.26M
InvestmentsAndAdvances10.18M38.87M200.56M391.91M
InvestmentinFinancialAssets10.18M38.87M200.56M391.91M
AvailableForSaleSecurities10.18M38.87M200.56M391.91M
NetPPE171.31M192.59M206.80M192.45M
AccumulatedDepreciation-72.29M-57.21M-41.39M-29.04M
GrossPPE243.60M249.80M248.19M221.49M
Leases101.47M101.93M99.40M92.53M
OtherProperties130.86M136.12M136.92M117.88M
MachineryFurnitureEquipment11.28M11.75M11.88M11.07M
Properties0.000.000.000.00
CurrentAssets278.00M334.97M415.98M518.83M
OtherCurrentAssets12.68M18.85M7.14M10.20M
PrepaidAssets9.07M14.52M13.90M18.75M
Receivables21.57M26.34M30.29M32.44M
ReceivablesAdjustmentsAllowances0.00-4.59M0.000.00
OtherReceivables20.41M24.52M27.80M32.07M
AccruedInterestReceivable1.09M1.55M2.21M
AccountsReceivable65.00K4.85M280.00K365.00K
AllowanceForDoubtfulAccountsReceivable-4.59M0.00
GrossAccountsReceivable65.00K4.85M280.00K
CashCashEquivalentsAndShortTermInvestments234.69M275.26M364.64M457.44M
OtherShortTermInvestments177.16M240.74M267.69M112.23M
CashAndCashEquivalents57.53M34.52M96.95M345.21M
Line Item2024-12-312023-12-312022-12-312021-12-31
FreeCashFlow-175.56M-228.37M-238.21M134.70M
IssuanceOfCapitalStock132.26M6.70M1.74M218.21M
CapitalExpenditure-2.44M-9.96M-30.72M-84.17M
InterestPaidSupplementalData6.56M7.28M23.12M21.64M
IncomeTaxPaidSupplementalData11.81M6.00M
EndCashPosition59.56M36.55M98.98M347.24M
BeginningCashPosition36.55M98.98M347.24M339.76M
ChangesInCash23.00M-62.43M-248.26M7.48M
FinancingCashFlow92.68M-34.97M-28.84M195.25M
CashFlowFromContinuingFinancingActivities92.68M-34.97M-28.84M195.25M
NetOtherFinancingCharges-41.09M-43.19M-33.39M-27.24M
ProceedsFromStockOptionExercised1.51M1.52M2.80M4.28M
NetCommonStockIssuance132.26M6.70M1.74M218.21M
CommonStockIssuance132.26M6.70M1.74M218.21M
InvestingCashFlow103.45M190.94M-11.93M-406.64M
CashFlowFromContinuingInvestingActivities103.45M190.94M-11.93M-406.64M
NetInvestmentPurchaseAndSale105.88M200.90M18.80M-322.47M
SaleOfInvestment296.02M287.47M203.67M175.68M
PurchaseOfInvestment-190.14M-86.56M-184.88M-498.14M
NetPPEPurchaseAndSale-2.44M-9.96M-30.72M-84.17M
PurchaseOfPPE-2.44M-9.96M-30.72M-84.17M
OperatingCashFlow-173.12M-218.41M-207.49M218.88M
CashFlowFromContinuingOperatingActivities-173.12M-218.41M-207.49M218.88M
ChangeInWorkingCapital5.53M-10.89M13.98M40.22M
ChangeInOtherWorkingCapital-33.00K-1.51M-1.17M-899.00K
ChangeInOtherCurrentLiabilities-10.69M-9.16M7.57M12.36M
ChangeInOtherCurrentAssets13.51M-3.19M4.73M-4.72M
ChangeInPayablesAndAccruedExpense-12.42M-339.00K-6.83M27.60M
ChangeInAccruedExpense-12.12M2.45M-25.62M29.91M
ChangeInPayable-292.00K-2.79M18.79M-2.30M
ChangeInAccountPayable-292.00K-2.79M18.79M-2.30M
ChangeInPrepaidAssets5.45M-620.00K4.85M-8.25M
ChangeInReceivables9.71M3.94M4.82M14.12M
ChangesInAccountReceivables9.71M3.94M4.82M14.12M
OtherNonCashItems7.42M-95.00K368.00K4.36M
StockBasedCompensation38.46M40.27M40.79M38.81M
ProvisionandWriteOffofAssets-5.00M0.000.00-2.57M
AssetImpairmentCharge2.10M0.000.00
AmortizationOfSecurities-4.14M687.00K4.71M5.84M
DepreciationAmortizationDepletion16.21M17.32M12.91M9.56M
DepreciationAndAmortization16.21M17.32M12.91M9.56M
OperatingGainsLosses-6.62M-2.21M79.00K-5.19M
GainLossOnInvestmentSecurities-6.62M-2.21M79.00K-5.19M
NetIncomeFromContinuingOperations-227.10M-263.49M-280.32M127.84M
SEC Filings

Recent 10-K, 10-Q, 8-K, and Form 4 (insider) filings.

Public Trades for RGNX
Date User Asset Broker Type Position Size Entry Price Patterns